Pediatric Genetics
Adakveo (crizanlizumab)
Adakveo (crizanlizumab) Hematology / Rare Diseases Adakveo No Crizanlizumab Prescription-only in the United States, Mexico, and Canada. [...]
Spinraza (nusinersen)
Spinraza (nusinersen) Neurology / Rare Genetic Disease Therapy Spinraza No Nusinersen Prescription-only Targeted [...]
Trikafta (elexacaftor / tezacaftor / ivacaftor)
Trikafta (elexacaftor / tezacaftor / ivacaftor) Cystic Fibrosis Therapy – CFTR Modulator Trikafta No Elexacaftor, Tezacaftor, Ivacaftor [...]