Rare Diseases
Omnitrope (somatropin)
Omnitrope (somatropin) Endocrinology / Hormone Therapy Omnitrope Yes (biosimilar to recombinant human growth hormone) Somatropin (recombinant [...]
Adakveo (crizanlizumab)
Adakveo (crizanlizumab) Hematology / Rare Diseases Adakveo No Crizanlizumab Prescription-only in the United States, Mexico, and Canada. [...]
Oxervate (cenegermin-bkbj)
Oxervate (cenegermin-bkbj) Ophthalmology / Rare Diseases Oxervate No Cenegermin-bkbj (recombinant human nerve growth factor) Prescription-only in [...]
Luxturna (voretigene neparvovec)
Luxturna (voretigene neparvovec-rzyl) Genetic Therapy / Ophthalmology Luxturna No generic or biosimilar available [...]
Spinraza (nusinersen)
Spinraza (nusinersen) Neurology / Rare Genetic Disease Therapy Spinraza No Nusinersen Prescription-only Targeted [...]
Trikafta (elexacaftor / tezacaftor / ivacaftor)
Trikafta (elexacaftor / tezacaftor / ivacaftor) Cystic Fibrosis Therapy – CFTR Modulator Trikafta No Elexacaftor, Tezacaftor, Ivacaftor [...]
